A Phase 3 Study of UX003 Recombinant Human Betaglucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis Type 7 (MPS 7)

NCT02230566 · clinicaltrials.gov ↗

PHASE3

Phase

COMPLETED

Status

12

Enrollment

INDUSTRY

Sponsor class

Conditions

MPS 7
Sly Syndrome
Mucopolysaccharidosis
MPS VII

Interventions

DRUG: UX003
OTHER: Placebo

Sponsor

Ultragenyx Pharmaceutical Inc