# Study of Gene Therapy Using a Lentiviral Vector to Treat X-linked Chronic Granulomatous Disease

> **NCT02234934** · PHASE1,PHASE2 · COMPLETED · sponsor: **University of California, Los Angeles** · enrollment: 10 (actual)

## Conditions studied

- Granulomatous Disease, Chronic, X-linked

## Interventions

- **BIOLOGICAL:** Lentiviral G1XCGD Gene Therapy

## Key facts

- **NCT ID:** NCT02234934
- **Lead sponsor:** University of California, Los Angeles
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2015-10-29
- **Primary completion:** 2024-09-01
- **Final completion:** 2024-12-01
- **Target enrollment:** 10 (ACTUAL)
- **Last updated:** 2025-05-02

## Collaborators

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## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02234934

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02234934, "Study of Gene Therapy Using a Lentiviral Vector to Treat X-linked Chronic Granulomatous Disease". Retrieved via AI Analytics 2026-06-29 from https://api.ai-analytics.org/clinical/NCT02234934. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
