# A Study of RO6885247 in Adult and Pediatric Patients With Spinal Muscular Atrophy (MOONFISH)

> **NCT02240355** · PHASE1 · TERMINATED · sponsor: **Hoffmann-La Roche** · enrollment: 9 (actual)

## Conditions studied

- Muscular Atrophy, Spinal

## Interventions

- **DRUG:** RO6885247
- **DRUG:** placebo

## Key facts

- **NCT ID:** NCT02240355
- **Lead sponsor:** Hoffmann-La Roche
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2014-11
- **Primary completion:** 2015-07
- **Final completion:** 2015-07
- **Target enrollment:** 9 (ACTUAL)
- **Why stopped:** There was an unexpected toxicology finding observed in the 39 week monkey study. Dosing was suspended, the study was put on hold and eventually terminated.
- **Last updated:** 2016-12-22


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02240355

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02240355, "A Study of RO6885247 in Adult and Pediatric Patients With Spinal Muscular Atrophy (MOONFISH)". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT02240355. Licensed CC0.

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