UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
Conditions
- Adrenoleukodystrophy
- Batten Disease
- Mucopolysaccharidosis II
- Leukodystrophy, Globoid Cell
- Leukodystrophy, Metachromatic
- Neimann Pick Disease
- Pelizaeus-Merzbacher Disease
- Sandhoff Disease
- Tay-Sachs Disease
- Brain Diseases, Metabolic, Inborn
- Alpha-Mannosidosis
- Sanfilippo Mucopolysaccharidoses
Interventions
Sponsor
Joanne Kurtzberg, MD