An Open Label Study of LMI070 (Branaplam) in Type 1 Spinal Muscular Atrophy (SMA)

NCT02268552 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

COMPLETED

Status

40

Enrollment

INDUSTRY

Sponsor class

Conditions

Spinal Muscular Atrophy

Interventions

DRUG: branaplam

Sponsor

Novartis Pharmaceuticals