# A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB

> **NCT02293382** · — · COMPLETED · sponsor: **Alexion Pharmaceuticals, Inc.** · enrollment: 30 (actual)

## Conditions studied

- MPS IIIB (Sanfilippo Syndrome)

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT02293382
- **Lead sponsor:** Alexion Pharmaceuticals, Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2013-07
- **Primary completion:** 2015-01
- **Final completion:** 2015-01
- **Target enrollment:** 30 (ACTUAL)
- **Last updated:** 2017-02-03


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02293382

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02293382, "A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB". Retrieved via AI Analytics 2026-06-08 from https://api.ai-analytics.org/clinical/NCT02293382. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
