ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)
Conditions
- Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)
- Amyloidosis, Hereditary
- Amyloid Neuropathies, Familial
- Amyloid Neuropathies
- Amyloidosis, Hereditary, Transthyretin-Related
- Familial Transthyretin Cardiac Amyloidosis
Interventions
- DRUG: Revusiran (ALN-TTRSC)
- DRUG: Sterile Normal Saline (0.9% NaCl)
Sponsor
Alnylam Pharmaceuticals