Long Term Safety Study of Orfadin Treatment in HT-1 Patients in Standard Clinical Care
NCT02320084
·
clinicaltrials.gov ↗
COMPLETED
Status
315
Enrollment
INDUSTRY
Sponsor class
Conditions
Hereditary Tyrosinemia, Type I
Interventions
DRUG:
Nitisinone
Sponsor
Swedish Orphan Biovitrum