Efficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1
NCT02323529
·
clinicaltrials.gov ↗
PHASE3
Phase
COMPLETED
Status
18
Enrollment
INDUSTRY
Sponsor class
Conditions
Hereditary Tyrosinemia, Type I
Interventions
DRUG:
Nitisinone
Sponsor
Swedish Orphan Biovitrum