# An Extension Study to Determine Safety and Efficacy for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093.

> **NCT02350816** · PHASE2 · TERMINATED · sponsor: **Shire** · enrollment: 17 (actual)

## Conditions studied

- Sanfilippo Syndrome
- Mucopolysaccharidosis (MPS)

## Interventions

- **DRUG:** HGT-1410

## Key facts

- **NCT ID:** NCT02350816
- **Lead sponsor:** Shire
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2015-04-08
- **Primary completion:** 2019-04-12
- **Final completion:** 2019-04-12
- **Target enrollment:** 17 (ACTUAL)
- **Why stopped:** Completion of follow-up period
- **Last updated:** 2021-06-11


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02350816

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02350816, "An Extension Study to Determine Safety and Efficacy for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093.". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT02350816. Licensed CC0.

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