# A Pilot Study of Pyridostigmine in Pompe Disease

> **NCT02357225** · EARLY_PHASE1 · TERMINATED · sponsor: **University of Florida** · enrollment: 2 (actual)

## Conditions studied

- Pompe Disease

## Interventions

- **DRUG:** Pyridostigmine Bromide

## Key facts

- **NCT ID:** NCT02357225
- **Lead sponsor:** University of Florida
- **Sponsor class:** OTHER
- **Phase:** EARLY_PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2015-08
- **Primary completion:** 2018-01-01
- **Final completion:** 2018-01-01
- **Target enrollment:** 2 (ACTUAL)
- **Why stopped:** The drug was ineffective in improving function in Pompe's disease
- **Last updated:** 2018-05-15


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02357225

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02357225, "A Pilot Study of Pyridostigmine in Pompe Disease". Retrieved via AI Analytics 2026-06-12 from https://api.ai-analytics.org/clinical/NCT02357225. Licensed CC0.

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