Antioxidant Therapy in RYR1-Related Congenital Myopathy
NCT02362425
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
63
Enrollment
NIH
Sponsor class
Conditions
Neuromuscular Disease
Interventions
DRUG:
N-acetylcysteine
DRUG:
Placebo
Sponsor
National Institute of Nursing Research (NINR)