# Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)

> **NCT02369731** · — · COMPLETED · sponsor: **PTC Therapeutics** · enrollment: 316 (actual)

## Conditions studied

- Muscular Dystrophy, Duchenne

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT02369731
- **Lead sponsor:** PTC Therapeutics
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2015-04-30
- **Primary completion:** 2025-03-31
- **Final completion:** 2025-03-31
- **Target enrollment:** 316 (ACTUAL)
- **Last updated:** 2026-02-24

## Collaborators

- [object Object]
- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02369731

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02369731, "Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)". Retrieved via AI Analytics 2026-05-26 from https://api.ai-analytics.org/clinical/NCT02369731. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
