# Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy

> **NCT02376816** · PHASE1 · COMPLETED · sponsor: **Jerry R. Mendell** · enrollment: 2 (actual)

## Conditions studied

- Duchenne Muscular Dystrophy

## Interventions

- **BIOLOGICAL:** rAAVrh74.MCK.micro-Dystrophin

## Key facts

- **NCT ID:** NCT02376816
- **Lead sponsor:** Jerry R. Mendell
- **Sponsor class:** OTHER
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** COMPLETED
- **Start date:** 2015-03
- **Primary completion:** 2017-09
- **Final completion:** 2017-09
- **Target enrollment:** 2 (ACTUAL)
- **Last updated:** 2017-11-24

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02376816

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02376816, "Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy". Retrieved via AI Analytics 2026-06-25 from https://api.ai-analytics.org/clinical/NCT02376816. Licensed CC0.

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