A Study of Multiple Doses of Nusinersen (ISIS 396443) Delivered to Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy
NCT02386553
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
25
Enrollment
INDUSTRY
Sponsor class
Conditions
Spinal Muscular Atrophy
Interventions
DRUG:
Nusinersen
Sponsor
Biogen