Phase 2 Tolerability and Effects of ALK-001 on Stargardt Disease
ENROLLING_BY_INVITATION
Status
Conditions
- Stargardt Disease
- Stargardt Macular Degeneration
- Stargardt Macular Dystrophy
- Autosomal Recessive Stargardt Disease 1 (ABCA4-related)
Interventions
- DRUG: ALK-001
- DRUG: Placebo
Sponsor
Alkeus Pharmaceuticals, Inc.