Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Treatment in Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7) Patients Less Than 5 Years of Age

NCT02418455 · clinicaltrials.gov ↗

PHASE2

Phase

COMPLETED

Status

8

Enrollment

INDUSTRY

Sponsor class

Conditions

Sly Syndrome
MPS VII
Mucopolysaccharidosis
Mucopolysaccharidosis VII

Interventions

DRUG: UX003

Sponsor

Ultragenyx Pharmaceutical Inc