Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular Dystrophy
NCT02420379
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
33
Enrollment
INDUSTRY
Sponsor class
Conditions
Duchenne Muscular Dystrophy (DMD)
Interventions
DRUG:
eteplirsen
Sponsor
Sarepta Therapeutics, Inc.