A Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Therapy in Subjects With Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7)

NCT02432144 · clinicaltrials.gov ↗

PHASE3

Phase

COMPLETED

Status

12

Enrollment

INDUSTRY

Sponsor class

Conditions

Sly Syndrome
MPS VII
Mucopolysaccharidosis
Mucopolysaccharidosis VII

Interventions

DRUG: UX003

Sponsor

Ultragenyx Pharmaceutical Inc