Gene Therapy for Transfusion Dependent Beta-thalassemia

NCT02453477 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

UNKNOWN

Status

10

Enrollment

OTHER

Sponsor class

Conditions

Beta-Thalassemia

Interventions

GENETIC: Autologous hematopoietic stem cells genetically modified with GLOBE lentiviral vector encoding for the human beta-globin gene

Sponsor

IRCCS San Raffaele

Collaborators

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