An Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease
Conditions
- Jansky-Bielschowsky Disease
- Batten Disease
- Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2
- CLN2 Disease
- CLN2 Disorder
Interventions
- BIOLOGICAL: BMN 190
- DEVICE: Intracerebroventricular (ICV) access device
Sponsor
BioMarin Pharmaceutical