Triheptanoin (UX007) to Treat Citrate Transporter Deficiency
NCT02500082
·
clinicaltrials.gov ↗
NO_LONGER_AVAILABLE
Status
OTHER
Sponsor class
Conditions
Citrate Transporter Deficiency
SLC13A5 Gene Mutation
Interventions
DRUG:
triheptanoin
Sponsor
Irina A Anselm