# Triheptanoin (UX007) to Treat Citrate Transporter Deficiency

> **NCT02500082** · — · NO_LONGER_AVAILABLE · sponsor: **Irina A Anselm**

## Conditions studied

- Citrate Transporter Deficiency
- SLC13A5 Gene Mutation

## Interventions

- **DRUG:** triheptanoin

## Key facts

- **NCT ID:** NCT02500082
- **Lead sponsor:** Irina A Anselm
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** EXPANDED_ACCESS
- **Status:** NO_LONGER_AVAILABLE
- **Start date:** —
- **Primary completion:** —
- **Final completion:** —
- **Target enrollment:** — (—)
- **Last updated:** 2016-01-28


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02500082

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02500082, "Triheptanoin (UX007) to Treat Citrate Transporter Deficiency". Retrieved via AI Analytics 2026-06-04 from https://api.ai-analytics.org/clinical/NCT02500082. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
