Pharmacological Treatment of a Rare Genetic Disease: N-acetylcysteine in Myopathy Associated Selenoprotein N-related Myopathy (SEPN1-RM)

NCT02505087 · clinicaltrials.gov ↗

PHASE2,PHASE3

Phase

TERMINATED

Status

7

Enrollment

OTHER

Sponsor class

Conditions

Selenoprotein N-related Myopathy

Interventions

DRUG: N-Acetylcysteine followed by Placebo
DRUG: Placebo followed by N-Acetylcysteine

Sponsor

Assistance Publique - Hôpitaux de Paris