Immune Modulation Therapy for Pompe Disease
NCT02525172
·
clinicaltrials.gov ↗
PHASE4
Phase
UNKNOWN
Status
8
Enrollment
OTHER
Sponsor class
Conditions
Pompe Disease
Interventions
DRUG:
Rituximab
DRUG:
intravenous immune globulin
DRUG:
Bortezomib
DRUG:
Methotrexate
Sponsor
National Taiwan University Hospital