Dose-Titration and Open-label Extension Study of SRP-4045 in Advanced Stage Duchenne Muscular Dystrophy (DMD) Patients
NCT02530905
·
clinicaltrials.gov ↗
PHASE1
Phase
COMPLETED
Status
12
Enrollment
INDUSTRY
Sponsor class
Conditions
Duchenne Muscular Dystrophy
Interventions
DRUG:
SRP-4045
DRUG:
Placebo
Sponsor
Sarepta Therapeutics, Inc.