Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy

NCT02559830 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

UNKNOWN

Status

50

Enrollment

OTHER

Sponsor class

Conditions

Metachromatic Leukodystrophy
Adrenoleukodystrophy

Interventions

GENETIC: transduced CD34+ hematopoietic stem cell

Sponsor

Shenzhen Second People's Hospital

Collaborators

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