# Tools for Therapeutic Evaluation in Charcot-Marie-Tooth Disease Type 1A: Outcome Measures and Biomarkers

> **NCT02596191** · NA · ACTIVE_NOT_RECRUITING · sponsor: **Assistance Publique Hopitaux De Marseille** · enrollment: 80 (estimated)

## Conditions studied

- Charcot-Marie-Tooth Disease Type 1A

## Interventions

- **OTHER:** Clinical evaluation
- **OTHER:** electrophysiological record
- **OTHER:** Muscle MRI
- **OTHER:** blood samples analysis

## Key facts

- **NCT ID:** NCT02596191
- **Lead sponsor:** Assistance Publique Hopitaux De Marseille
- **Sponsor class:** OTHER
- **Phase:** NA
- **Study type:** INTERVENTIONAL
- **Status:** ACTIVE_NOT_RECRUITING
- **Start date:** 2016-06-06
- **Primary completion:** 2026-06-05
- **Final completion:** 2027-12-05
- **Target enrollment:** 80 (ESTIMATED)
- **Last updated:** 2025-06-27


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02596191

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02596191, "Tools for Therapeutic Evaluation in Charcot-Marie-Tooth Disease Type 1A: Outcome Measures and Biomarkers". Retrieved via AI Analytics 2026-05-24 from https://api.ai-analytics.org/clinical/NCT02596191. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
