Study of ORGN001 (Formerly ALXN1101) in Neonates, Infants and Children With Molybdenum Cofactor Deficiency (MOCD) Type A

NCT02629393 · clinicaltrials.gov ↗
PHASE2,PHASE3
Phase
COMPLETED
Status
5
Enrollment
INDUSTRY
Sponsor class

Conditions

Interventions

Sponsor

Origin Biosciences