Study of ORGN001 (Formerly ALXN1101) in Neonates, Infants and Children With Molybdenum Cofactor Deficiency (MOCD) Type A
NCT02629393
·
clinicaltrials.gov ↗
PHASE2,PHASE3
Phase
COMPLETED
Status
5
Enrollment
INDUSTRY
Sponsor class
Conditions
Molybdenum Cofactor Deficiency, Type A
Interventions
DRUG:
ORGN001 (formerly ALXN1101)
Sponsor
Origin Biosciences