Ascending Dose Study of Genome Editing by Zinc Finger Nuclease Therapeutic SB-FIX in Subjects With Severe Hemophilia B
NCT02695160
·
clinicaltrials.gov ↗
PHASE1
Phase
TERMINATED
Status
1
Enrollment
INDUSTRY
Sponsor class
Conditions
Hemophilia B
Interventions
BIOLOGICAL:
SB-FIX
Sponsor
Sangamo Therapeutics