# A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects

> **NCT02704273** · — · COMPLETED · sponsor: **Astellas Gene Therapies** · enrollment: 34 (actual)

## Conditions studied

- X-linked Myotubular Myopathy

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT02704273
- **Lead sponsor:** Astellas Gene Therapies
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2016-07
- **Primary completion:** 2019-09
- **Final completion:** 2019-09
- **Target enrollment:** 34 (ACTUAL)
- **Last updated:** 2022-07-29


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02704273

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02704273, "A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects". Retrieved via AI Analytics 2026-06-03 from https://api.ai-analytics.org/clinical/NCT02704273. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
