# Gene Transfer Clinical Trial for Duchenne Muscular Dystrophy Using rAAVrh74.MCK.GALGT2

> **NCT02704325** · PHASE1,PHASE2 · WITHDRAWN · sponsor: **Kevin Flanigan**

## Conditions studied

- Duchenne Muscular Dystrophy

## Interventions

- **BIOLOGICAL:** rAAVrh74.MCK.GALGT2
- **OTHER:** PLACEBO (Saline)

## Key facts

- **NCT ID:** NCT02704325
- **Lead sponsor:** Kevin Flanigan
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** WITHDRAWN
- **Start date:** 2016-04
- **Primary completion:** 2018-07
- **Final completion:** 2020-02
- **Target enrollment:** 0 (ACTUAL)
- **Last updated:** 2018-02-06


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02704325

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02704325, "Gene Transfer Clinical Trial for Duchenne Muscular Dystrophy Using rAAVrh74.MCK.GALGT2". Retrieved via AI Analytics 2026-06-13 from https://api.ai-analytics.org/clinical/NCT02704325. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
