A Treatment Study of Mucopolysaccharidosis Type IIIB
NCT02754076
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
23
Enrollment
INDUSTRY
Sponsor class
Conditions
MPS III B
Mucopolysaccharidosis Type IIIB
Interventions
DRUG:
AX 250
Sponsor
Allievex Corporation