Clearing Lungs With ENaC Inhibition in Primary Ciliary Dyskinesia
Conditions
- Primary Ciliary Dyskinesia
Interventions
- DRUG: VX-371
- DRUG: Hypertonic Saline
- DRUG: Placebo (0.17% saline)
- DRUG: VX-371 + HS
- DRUG: Ivacaftor
Sponsor
Parion Sciences
Collaborators