A Study to Assess the Safety and Tolerability of Lucerastat in Subjects With Fabry Disease
NCT02930655
·
clinicaltrials.gov ↗
PHASE1
Phase
COMPLETED
Status
14
Enrollment
INDUSTRY
Sponsor class
Conditions
Fabry Disease
Interventions
DRUG:
Lucerastat
DRUG:
Enzyme replacement therapy (ERT)
Sponsor
Idorsia Pharmaceuticals Ltd.