In Utero Hematopoietic Stem Cell Transplantation for Alpha-thalassemia Major (ATM)
Stopped Enrollment ended early due to interim data suggesting a lack of efficacy. Interim data did demonstrate that IUHSCT was safe and well tolerated, but the PI and DSMB agreed that enrollment should not continue under the current treatment protocol.
Conditions
- Alpha Thalassemia Major
- Hemoglobinopathy; With Thalassemia
- Hemoglobinopathies
- Fetal Anemia
- Fetal Hydrops
- Alpha; Thalassemia
- Thalassemia Major
- Thalassemia Alpha
- A-Thalassemia
Interventions
- BIOLOGICAL: in utero hematopoietic stem cell transplantation
Sponsor
University of California, San Francisco
Collaborators