# Natural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)

> **NCT02998710** · — · RECRUITING · sponsor: **Travere Therapeutics, Inc.** · enrollment: 150 (estimated)

## Conditions studied

- Homocystinuria Due to CBS Deficiency

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT02998710
- **Lead sponsor:** Travere Therapeutics, Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** RECRUITING
- **Start date:** 2017-01
- **Primary completion:** 2026-04
- **Final completion:** 2026-08
- **Target enrollment:** 150 (ESTIMATED)
- **Last updated:** 2024-11-22


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT02998710

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT02998710, "Natural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT02998710. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*