A Study of Risdiplam (RO7034067) in Adult and Pediatric Participants With Spinal Muscular Atrophy
NCT03032172
·
clinicaltrials.gov ↗
PHASE2
Phase
COMPLETED
Status
174
Enrollment
INDUSTRY
Sponsor class
Conditions
Spinal Muscular Atrophy
Interventions
DRUG:
Risdiplam
Sponsor
Hoffmann-La Roche