Efficacy and Safety Study of Fosmetpantotenate (RE-024) in PKAN Participants
Stopped The study was terminated since fosmetpantotenate did not show statistically significant effects or clinical benefits during the double-blind period.
Conditions
- Pantothenate Kinase-Associated Neurodegeneration
Interventions
- DRUG: Fosmetpantotenate
- DRUG: Placebo
Sponsor
Travere Therapeutics, Inc.