# Trial Readiness and Endpoint Assessment in Congenital Myotonic Dystrophy

> **NCT03059264** · — · COMPLETED · sponsor: **Virginia Commonwealth University** · enrollment: 100 (actual)

## Conditions studied

- Congenital Myotonic Dystrophy

## Interventions

- **OTHER:** Natural history

## Key facts

- **NCT ID:** NCT03059264
- **Lead sponsor:** Virginia Commonwealth University
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2016-12-14
- **Primary completion:** 2021-12-08
- **Final completion:** 2025-01-27
- **Target enrollment:** 100 (ACTUAL)
- **Last updated:** 2025-03-11

## Collaborators

- [object Object]
- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03059264

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03059264, "Trial Readiness and Endpoint Assessment in Congenital Myotonic Dystrophy". Retrieved via AI Analytics 2026-05-23 from https://api.ai-analytics.org/clinical/NCT03059264. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
