# Cardiopulmonary Exercise Test to Quantify Enzyme Replacement Response in Pediatric Pompe Disease

> **NCT03147664** · — · COMPLETED · sponsor: **Rambam Health Care Campus** · enrollment: 5 (actual)

## Conditions studied

- Enzyme Replacement Therapy in Pompe Disease

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT03147664
- **Lead sponsor:** Rambam Health Care Campus
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2014-01-01
- **Primary completion:** 2014-04-30
- **Final completion:** 2017-03-30
- **Target enrollment:** 5 (ACTUAL)
- **Last updated:** 2017-05-16


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03147664

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03147664, "Cardiopulmonary Exercise Test to Quantify Enzyme Replacement Response in Pediatric Pompe Disease". Retrieved via AI Analytics 2026-05-27 from https://api.ai-analytics.org/clinical/NCT03147664. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
