Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I, II, and VI
ACTIVE_NOT_RECRUITING
Status
Conditions
- Mucopolysaccharidosis I
- Mucopolysaccharidosis II
- Mucopolysaccharidosis VI
Interventions
- DRUG: Adalimumab Injection [Humira]
- DRUG: Saline Solution for Injection
Sponsor
Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center
Collaborators