A Study of AT132 in Young Children With X-Linked Myotubular Myopathy (XLMTM)

NCT03199469 · clinicaltrials.gov ↗

PHASE2,PHASE3

Phase

ACTIVE_NOT_RECRUITING

Status

27

Enrollment

INDUSTRY

Sponsor class

Conditions

X-Linked Myotubular Myopathy

Interventions

GENETIC: Resamirigene bilparvovec

Sponsor

Astellas Gene Therapies