# Natural History of Atypical Morquio A Disease

> **NCT03204370** · — · COMPLETED · sponsor: **GOIZET** · enrollment: 7 (actual)

## Conditions studied

- Mucopolysaccharidosis IV A

## Interventions

- **DRUG:** Elosulfase Alfa 1 MG/ML Intravenous Solution [VIMIZIM]

## Key facts

- **NCT ID:** NCT03204370
- **Lead sponsor:** GOIZET
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2018-02-01
- **Primary completion:** 2025-02-01
- **Final completion:** 2025-09-01
- **Target enrollment:** 7 (ACTUAL)
- **Last updated:** 2025-10-03

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03204370

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03204370, "Natural History of Atypical Morquio A Disease". Retrieved via AI Analytics 2026-05-25 from https://api.ai-analytics.org/clinical/NCT03204370. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
