# Eltrombopag for People With Fanconi Anemia

> **NCT03206086** · PHASE2 · ACTIVE_NOT_RECRUITING · sponsor: **National Heart, Lung, and Blood Institute (NHLBI)** · enrollment: 25 (actual)

## Conditions studied

- Fanconi Anemia

## Interventions

- **DRUG:** Eltrombopag

## Key facts

- **NCT ID:** NCT03206086
- **Lead sponsor:** National Heart, Lung, and Blood Institute (NHLBI)
- **Sponsor class:** NIH
- **Phase:** PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** ACTIVE_NOT_RECRUITING
- **Start date:** 2018-11-02
- **Primary completion:** 2025-08-01
- **Final completion:** 2028-08-01
- **Target enrollment:** 25 (ACTUAL)
- **Last updated:** 2025-08-24


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03206086

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03206086, "Eltrombopag for People With Fanconi Anemia". Retrieved via AI Analytics 2026-05-24 from https://api.ai-analytics.org/clinical/NCT03206086. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
