Extension Study of RA101495 for Patients With PNH Who Have Completed a Zilucoplan (RA101495) Clinical Study
Stopped After careful consideration, UCB has decided to no longer pursue PNH as a potential indication for zilucoplan.
Conditions
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
Interventions
- DRUG: Zilucoplan (RA101495)
Sponsor
Ra Pharmaceuticals, Inc.