# Farber Disease Natural History Study

> **NCT03233841** · — · COMPLETED · sponsor: **Sumitomo Pharma Switzerland GmbH** · enrollment: 45 (actual)

## Conditions studied

- Farber Disease
- Farber's Disease
- Farber Lipogranulomatosis
- Acid Ceramidase Deficiency
- Ceramidase Deficiency
- N-Laurylsphingosine Deacylase Deficiency
- ASAH1 Mutation

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT03233841
- **Lead sponsor:** Sumitomo Pharma Switzerland GmbH
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2017-11-22
- **Primary completion:** 2019-10-12
- **Final completion:** 2019-12-09
- **Target enrollment:** 45 (ACTUAL)
- **Last updated:** 2020-01-18


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT03233841

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT03233841, "Farber Disease Natural History Study". Retrieved via AI Analytics 2026-05-23 from https://api.ai-analytics.org/clinical/NCT03233841. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
