Gene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR)
NCT03252847
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
49
Enrollment
INDUSTRY
Sponsor class
Conditions
X-Linked Retinitis Pigmentosa
Interventions
GENETIC:
AAV5-RPGR
Sponsor
MeiraGTx UK II Ltd
Collaborators
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