Long-Term Follow-Up Gene Therapy Study for Achromatopsia CNGB3 and CNGA3

Stopped Strategic decision to not further develop AAV8-hCARp.hCNGB3 and AAV8-hG1.7p.coCNGA3. The decision is not due to safety concerns.

Conditions

• Achromatopsia

Interventions

• BIOLOGICAL: Prior exposure to AAV-CNGA3 or AAV-CNGB3

Sponsor

MeiraGTx UK II Ltd