Safety and Efficacy of rAAV2tYF-GRK1-RPGR in Subjects With X-linked Retinitis Pigmentosa Caused by RPGR Mutations
ACTIVE_NOT_RECRUITING
Status
Conditions
- X-Linked Retinitis Pigmentosa
Interventions
- BIOLOGICAL: rAAV2tYF-GRK1-RPGR
Sponsor
Beacon Therapeutics